Avidity Biosciences Says It Is Opening Up New Therapeutic Field, Precision Cardiology, To Address Root Cause Of Genetic Diseases Of Heart

Atrium Therapeutics

Atrium Therapeutics

RNA

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Avidity is advancing its first two new wholly-owned precision cardiology development candidates targeting rare genetic cardiomyopathies: AOC 1086 targeting PLN (phospholamban) cardiomyopathy and AOC 1072 targeting PRKAG2 (Protein Kinase AMP-activated non-catalytic subunit Gamma 2) Syndrome. 

In addition, Avidity shared preclinical data from next-generation technology innovations demonstrating improved siRNA delivery and increased durability.