BioMarin says VOXZOGO lifts height SDS 0.72 over three years in hypochondroplasia study at ENDO 2026

BioMarin Pharmaceutical Inc.

BioMarin Pharmaceutical Inc.

BMRN

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  • BioMarin highlighted new VOXZOGO data in hypochondroplasia, presented at ENDO 2026, showing sustained growth benefits over three years with a favorable safety profile.
  • The update supports plans to file a U.S. supplemental NDA for VOXZOGO in hypochondroplasia in Q3 2026, following positive Phase 3 topline results.
  • Phase 1 results for investigational BMN 333, also presented at ENDO 2026, supported the potential for weekly dosing in achondroplasia with tolerable safety.
  • Enrollment has started in a registration-enabling Phase 2/3 study for BMN 333; a dose-finding update is expected in 2027.


Disclaimer: This news brief was created by Public Technologies (PUBT) using generative artificial intelligence. While PUBT strives to provide accurate and timely information, this AI-generated content is for informational purposes only and should not be interpreted as financial, investment, or legal advice. BioMarin Pharmaceutical Inc. published the original content used to generate this news brief via PR Newswire (Ref. ID: 202606160905PR_NEWS_USPR_____SF83044) on June 16, 2026, and is solely responsible for the information contained therein.