BRIEF-Design Therapeutics Announces Four-Week IV Data From The RESTORE-FA Trial Of DT-216P2 Demonstrating Clinical Improvements And Comprehensive Biomarker Activity In Friedreich Ataxia

Design Therapeutics, Inc.

Design Therapeutics, Inc.

DSGN

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- Design Therapeutics Inc DSGN.O:

  • DESIGN THERAPEUTICS ANNOUNCES FOUR-WEEK IV DATA FROM THE RESTORE-FA TRIAL OF DT-216P2 DEMONSTRATING CLINICAL IMPROVEMENTS AND COMPREHENSIVE BIOMARKER ACTIVITY IN FRIEDREICH ATAXIA

  • DESIGN THERAPEUTICS INC - DT-216P2 GENERALLY WELL-TOLERATED WITH NO SERIOUS ADVERSE EVENTS REPORTED

  • DESIGN THERAPEUTICS INC - DT-216P2 IMPROVES PATIENT-REPORTED FATIGUE BY OVER FIVE POINTS AFTER FOUR WEEKS

  • DESIGN THERAPEUTICS INC - TO PURSUE REGISTRATIONAL DEVELOPMENT FOR DT-216P2, UPDATE IN Q4 2026

  • DESIGN THERAPEUTICS INC - DT-216P2 AT 1 MPK IMPROVES M-FARS BY 6.4 POINTS AND UPRIGHT STABILITY BY 2.7 POINTS

Source text: ID:nGNX341dL2

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