BRIEF-Proqr Announces Positive Phase 1 Target Engagement Data For Ax-0810, Establishing First Clinical Validation Of The Axiomer Rna Editing Platform

ProQR Therapeutics N.V.

ProQR Therapeutics N.V.

PRQR

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- ProQR Therapeutics NV PRQR.O:

  • PROQR ANNOUNCES POSITIVE PHASE 1 TARGET ENGAGEMENT DATA FOR AX-0810, ESTABLISHING FIRST CLINICAL VALIDATION OF THE AXIOMER RNA EDITING PLATFORM

  • PROQR THERAPEUTICS NV - AX-810 SHOWS FAVORABLE SAFETY PROFILE AND EIGHT-WEEK HALF-LIFE

  • PROQR THERAPEUTICS NV - AX-2911 FIRST-IN-HUMAN IIT IN CHINA EXPECTED FIRST HALF 2027

  • PROQR THERAPEUTICS NV - AX-422 CTA FILING FOR MPS1 EXPECTED EARLY 2027 WITH INITIAL DATA FIRST HALF 2027

  • PROQR THERAPEUTICS NV - PHASE 2 PROGRAM EXPECTED TO START MID-2027 WITH INTERIM DATA BY MID-2028

Source text: ID:nGNX7mH6gl

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