UPDATE 1-Regenxbio's muscle disorder therapy meets main goal in late-stage study
REGENXBIO, Inc. RGNX | 0.00 |
Adds details thorughout
May 14 (Reuters) - Regenxbio RGNX.O said on Thursday that its experimental therapy to treat a muscle-wasting disorder met the main goal in a late-stage study.
Shares of the company were halted in premarket trading.
The Rockville, Maryland-based company said 93% of patients with Duchenne muscular dystrophy treated with the therapy RGX-202 reached the expected level of a key protein known as microdystrophin 12 weeks after treatment.
Microdystrophin is a shortened version of dystrophin, the muscle-protecting protein missing or defective in people with the disorder.
The company said the drug was well-tolerated. It plans to seek accelerated approval in 2027.
